FDA Grants Orphan Drug Designation to AND017 for the Treatment of Sickle Cell Disease
October 28th 2024Results demonstrating safety and efficacy in those with anemia in non-dialysis dependent chronic kidney disease and anemia in dialysis-dependent chronic kidney disease were presented at the 2024 American Society of Nephrology Kidney Week.
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FDA Grants Orphan Drug Designation to MDL-101 for Congenital Muscular Dystrophy Type 1a
Published: October 25th 2024 | Updated: October 25th 2024Congenital muscular dystrophy type 1a is a severe, early-onset condition that currently has no treatment, but MDL-101 may serve as a 1-time, durable treatment option.
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Real-World Evidence Presented at IDWeek Demonstrates Efficacy of CAB LA When Used for HIV PrEP
October 23rd 2024Cabotegravir long-acting when used for HIV pre-exposure prophylaxis (PrEP) showed adherence, effectiveness, and improvements in quality of life by those who received the injection.
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FDA Approves Sodium Oxybate to Treat Cataplexy or EDS in Pediatric Patients With Narcolepsy
Published: October 17th 2024 | Updated: October 17th 2024Patients aged 7 years and older can now be treated for their cataplexy or excessive daytime sleepiness with the extended-release oral formulation.
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FDA Approves Foscarbidopa/Foslevodopa for Motor Fluctuations in Adults With Parkinson Disease
Published: October 17th 2024 | Updated: October 17th 2024This approval makes foscarbidopa/foslevodopa the first and only subcutaneous 24-hour infusion of levodopa-based therapy for adults with Parkinson disease.
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Increases in Pre-Term Birth Rates Observed in All Races, Higher Increases in Minority Groups
October 9th 2024The highest pre-term birth rates were consistently observed among those who were Black, American Indian or Alaska Native, or Native Hawaiian or other Pacific islander with public insurance.
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