Treatment for Patients With Congenital Plasminogen Deficiency With Airway Obstruction and Respiratory Distress

Pharmacy Times^® interviewed Charles Nakar, MD and Amy Shapiro, MD, both pediatric hematologist-oncologists at the Indiana Hemophilia & Thrombosis Center, on their presentation at the 62nd ASH Annual Meeting and Exposition. The presentation discusses research into acute airway obstruction in 4 pediatric patients with congenital plasminogen deficiency treated with intravenous plasminogen replacement therapy under an expanded access protocol.

In this video, Shapiro explains what the treatment options available are for patients with congenital plasminogen deficiency with airway obstruction and respiratory distress, and whether it would differ from treatment for patients with congenital plasminogen deficiency without airway obstruction and respiratory distress.